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CRISPR/Cas with ribonucleoprotein complexes and transiently selected telomere vectors allows highly efficient marker-free and multiple genome editing in Botrytis cinerea2020 PLoS Pathogens article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 1 patent
Thomas Leisen, Fabian Bietz, J.A. Werner, Alex Wegner, Ulrich Schaffrath, David Scheuring, +4 more
128citations -
Large-scale genome editing based on high-capacity adenovectors and CRISPR-Cas9 nucleases rescues full-length dystrophin synthesis in DMD muscle cells2022 Nucleic Acids Research article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Francesca Tasca, Marcella Brescia, Qian Wang, Jin Liu, Josephine M. Janssen, Károly Szuhai, +1 more
21citations -
Precise homology-directed installation of large genomic edits in human cells with cleaving and nicking high-specificity Cas9 variants2023 Nucleic Acids Research article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Qian Wang, Jin Liu, Josephine M. Janssen, Manuel A.F.V. Gonçalves
19citations -
Comparative Analysis of Methods for Assessing On-Target Gene Editing Efficiencies2025 Methods and Protocols article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Bing Yao, Qiangbing Yang, Manuel A.F.V. Gonçalves, Raymond Michel Schiffelers, Joost P. G. Sluijter, Zhiyong Lei
7citations -
Anti‐C1q autoantibodies may not serve as an adequate biomarker for lung manifestations in systemic sclerosis: a single‐centre, cross‐sectional study2021 British Journal of Dermatology article Medicine Systemic Sclerosis and Related Diseases Open access
Douwe J. Dijkstra, Sophie I E Liem, Nina Marijn van Leeuwen, Cynthia M. Fehres, Jeska Kirsten De Vries-Bouwstra, Leendert Adrianus Trouw
1citations -
A Small Key for a Heavy Door: Genetic Therapies for the Treatment of Hemoglobinopathies2021 Frontiers in Genome Editing article Medicine Hemoglobinopathies and Related Disorders Open access cited by 4 patents
Hidde A. Zittersteijn, Cornelis L. Harteveld, Stefanie Klaver-Flores, Arjan C. Lankester, Rob C. Hoeben, Frank J. T. Staal, +1 more
19citations -
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi2023 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Alessia Cavazza, Ayal Hendel, Rasmus Otkjær Bak, Paula Rı́o, Marc Güell, Duško Lainšček, +33 more
12citations -
CD44-targeted lipid nanoparticles for enhanced CRISPR/Cas9 delivery in cancer gene editing2026 Journal of Controlled Release article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access
Ye Zeng, Gangyin Zhao, Shidi Wu, Hu Bochuan, Gabriel Forn‐Cuní, Renzo A. Knol, +3 more
6citations -
M Protein Interference in Renal Function Assays: A Quest for True Kidney Function2025 The Journal of Applied Laboratory Medicine article Health Professions Clinical Laboratory Practices and Quality Control Open access
Michelle P. van der Helm, Brigitte A. Wevers, Cees van Beek, Paul W. Schenk, Angela Bikker
2citations -
Evaluation of in vitro liver models and non-human primates for predicting ADAR RNA editing efficiency in human liver2025 Scientific Reports article Biochemistry, Genetics and Molecular Biology RNA regulation and disease Open access
Mònica Aguilà, Nicole H.P. Cnubben, David A. Parfitt, Bruno Albuquerque, Peter C. de Visser, Marlieke Molendijk, +1 more
1citations -
Prevalence and determinants of over- and undertreatment among users of antihypertensive drugs in the general population: the Rhineland Study2023 European Journal of Preventive Cardiology article Medicine Blood Pressure and Hypertension Studies Open access
Nersi Alaeddin, Gökhan Pehlivan, Monique M.B. Breteler, Folgerdiena M. de Vries
1citations -
Protocol for non-viral HDR-based CRISPR/Cas9 platform for small custom editing in primary T cells2026 Frontiers in Genome Editing article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Katariina Mamia, Anniken Solveig Matheson Sollano, Vanja Lundberg, Svetlana Vakkilainen, Eliisa Kekäläinen, Camilla Schalin-Jäntti, +6 more
0citations -
Review of A revolution in fragments. Traversing scales of justice, ideology and practice in Bolivia0citations
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CRISPR-Cas9 induces large structural variants at on-target and off-target sites in vivo that segregate across generations2022 Nature Communications article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 1 patent
Ida Höijer, Anastasia Emmanouilidou, Rebecka Östlund, Robin van Schendel, Selma Bozorgpana, Marcel Tijsterman, +4 more
196citations -
Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome2021 EMBO Molecular Medicine article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 7 patents
Valentina Vavassori, Elisabetta Mercuri, Genni Enza Marcovecchio, Maria Carmina Castiello, Giulia Schiroli, Luisa Albano, +17 more
53citations -
PLGA-Nanoparticles for Intracellular Delivery of the CRISPR-Complex to Elevate Fetal Globin Expression in Erythroid Cells2020 Biomaterials article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access cited by 1 patent
Luis Javier Cruz, Thamar van Dijk, Olena Vepris, Tracy M.W.Y. Li, Timo Schomann, Fabio Baldazzi, +5 more
49citations -
Epigenetic editing at individual age-associated CpGs affects the genome-wide epigenetic aging landscape2025 Nature Aging article Biochemistry, Genetics and Molecular Biology Epigenetics and DNA Methylation Open access
Sven Liesenfelder, Mohamed H. Elsafi Mabrouk, Jessica Iliescu, Monica Varona Baranda, Athanasia Mizi, Juan-Felipe Perez-Correa, +3 more
39citations -
Preservation stress resistance of melanin deficient conidia from Paecilomyces variotii and Penicillium roqueforti mutants generated via CRISPR/Cas9 genome editing2021 Fungal Biology and Biotechnology article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Sjoerd J. Seekles, Pepijn Teunisse, Maarten Punt, Tom van den Brule, Jan Dijksterhuis, Jos A. M. P. Houbraken, +2 more
35citations