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Successful Preclinical Development of Gene Therapy for Recombinase-Activating Gene-1-Deficient SCID2020 Molecular Therapy — Methods & Clinical Development article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 3 patents
Laura García-Pérez, Marja C.J.A. van Eggermond, Lieke van Roon, Sandra A. Vloemans, Martijn Cordes, Axel Schambach, +16 more
58citations -
Molecular characterization of Cdh12-SCON conditional knockout mice reveals unexpected splicing changes2026 Transgenic Research article Biochemistry, Genetics and Molecular Biology RNA Research and Splicing Open access
Mayke A C Ten Hoor, Margot M. L. Linssen, Conny M. Brouwers, Jill W. C. Claassens, Jaap Mulder, Peter Hohenstein
0citations -
High sorbic acid resistance of Penicillium roqueforti is mediated by the SORBUS gene cluster2022 PLoS Genetics article Biochemistry, Genetics and Molecular Biology Fungal and yeast genetics research Open access
Maarten Punt, Sjoerd J. Seekles, Jisca L. van Dam, Connor de Adelhart Toorop, Raithel R. Martina, Jos A. M. P. Houbraken, +3 more
15citations -
High sorbic acid resistance of Penicillium roqueforti is mediated by the SORBUS gene cluster2022 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Fungal and yeast genetics research Open access
Maarten Punt, Sjoerd J. Seekles, Jisca L. van Dam, Connor de Adelhart Toorop, Raithel R. Martina, Jos A. M. P. Houbraken, +3 more
2citations -
SCON—a Short Conditional intrON for conditional knockout with one-step zygote injection2022 Experimental & Molecular Medicine article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Szu-Hsien Sam Wu, Heetak Lee, Réka Szép-Bakonyi, Gabriele Colozza, Ayse Boese, Krista R. Gert, +10 more
8citations -
Smad4 and TGFβ1 dependent gene expression signatures in conditional intestinal adenoma, organoids and colorectal cancer2025 Scientific Reports article Biochemistry, Genetics and Molecular Biology TGF-β signaling in diseases Open access
Mirvat Surakhy, David Barnes, Emma J. Carter, Jennifer Hughes, Claudia Bühnemann, Sabina Sanegre, +4 more
2citations -
Author Correction: SCON—a Short Conditional intrON for conditional knockout with one-step zygote injection2023 Experimental & Molecular Medicine erratum Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Szu-Hsien Sam Wu, Heetak Lee, Réka Szép-Bakonyi, Gabriele Colozza, Ayse Boese, Krista R. Gert, +10 more
0citations -
CRISPR-Induced Knockout of Ubiquitin Ligase Cullin 3 in Human Proximal Tubule Cells2021 Journal of the American Society of Nephrology conference-abstract Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering
Turgay Saritas, Lu Chen, Susanne Maria Ziegler, Nazanin Kabgani, Christoph Kuppe, Jürgen Floege, +2 more
0citations -
PFKFB3 gene deletion in endothelial cells inhibits intraplaque angiogenesis and lesion formation in a murine model of venous bypass grafting2021 Angiogenesis article Immunology and Microbiology Atherosclerosis and Cardiovascular Diseases Open access
Paola Perrotta, Margreet R. de Vries, Bart Peeters, Pieter‐Jan Guns, Guido R.Y. De Meyer, Paul H.A. Quax, +1 more
30citations -
Interventional gene targeting of the cell cycle regulator Cyclin E1 during hepatocarcinogenesis attenuates cancer progression with limited proliferation, stemness traits and micro-metastasis2020 Zeitschrift für Gastroenterologie conference-paper Medicine Hepatocellular Carcinoma Treatment and Prognosis
Marlene Sophia Kohlhepp, Antje Mohs, Christian Penners, Daniela Lambertz, Frank Tacke, Christian Trautwein, +1 more
0citations -
PRMT4 inhibitor TP-064 impacts both inflammatory and metabolic processes without changing the susceptibility for early atherosclerotic lesions in male apolipoprotein E knockout mice2021 Atherosclerosis article Biochemistry, Genetics and Molecular Biology Cancer-related gene regulation Open access
Yiheng Zhang, Robin A.F. Verwilligen, Timothy J. P. Sijsenaar, Miranda Van Eck, Menno Hoekstra
14citations -
GRHL2-controlled gene expression networks in luminal breast cancer2023 Cell Communication and Signaling article Biochemistry, Genetics and Molecular Biology Estrogen and related hormone effects Open access
Zi Wang, Bircan Coban, Haoyu Wu, Jihed Chouaref, Lucia Daxinger, Michelle T. Paulsen, +4 more
32citations -
A seven-membered cell wall related transglycosylase gene family in Aspergillus niger is relevant for cell wall integrity in cell wall mutants with reduced α-glucan or galactomannan2020 The Cell Surface article Biochemistry, Genetics and Molecular Biology Fungal and yeast genetics research Open access
Tim M. van Leeuwe, Jasper Wattjes, Anna Niehues, Gabriel Forn‐Cuní, Nicholas Geoffrion, Hugo Mélida, +7 more
23citations -
Preclinical efficacy and safety of adeno-associated virus 5 alpha-galactosidase: A gene therapy for Fabry disease2024 Molecular Therapy — Methods & Clinical Development article Medicine Lysosomal Storage Disorders Research Open access
Jolanda M.P. Liefhebber, Giso Brasser, Elisabeth A. Spronck, Roelof Ottenhoff, Lieke Paerels, Maria J. Ferraz, +6 more
9citations -
Gene Supplementation of MYO7A or activation of Myo7b for treatment of Usher syndrome 1B2026 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access
David Manuel Mittas, Dina Yehia Otify, Zoran Gavrilov, Thomas Heigl, Jan Suchomski, Paulina Deltuvaite, +27 more
0citations