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Impact of Genome Editing delivery tools on target cells: Training School Report2026 Zenodo (CERN European Organization for Nuclear Research) report Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Carla Fuster‐García, Manuel Rhiel, Duško Lainšček, Manuel A.F.V. Gonçalves, Hildegard Büning, Marcello Maresca, +5 more
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CRISPR-Cas9 induces large structural variants at on-target and off-target sites in vivo that segregate across generations2021 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
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Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group2025 Molecular Therapy — Nucleic Acids review Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Alessia Cavazza, Francisco Javier Molina-Estévez, Álvaro Plaza Reyes, Víctor Ronco-Díaz, Asma Naseem, Špela Malenšek, +30 more
76citations -
A Small Key for a Heavy Door: Genetic Therapies for the Treatment of Hemoglobinopathies2021 Frontiers in Genome Editing article Medicine Hemoglobinopathies and Related Disorders Open access cited by 4 patents
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19citations -
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi2023 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
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12citations -
CD44-targeted lipid nanoparticles for enhanced CRISPR/Cas9 delivery in cancer gene editing2026 Journal of Controlled Release article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access
Ye Zeng, Gangyin Zhao, Shidi Wu, Hu Bochuan, Gabriel Forn‐Cuní, Renzo A. Knol, +3 more
6citations -
M Protein Interference in Renal Function Assays: A Quest for True Kidney Function2025 The Journal of Applied Laboratory Medicine article Health Professions Clinical Laboratory Practices and Quality Control Open access
Michelle P. van der Helm, Brigitte A. Wevers, Cees van Beek, Paul W. Schenk, Angela Bikker
2citations -
Evaluation of in vitro liver models and non-human primates for predicting ADAR RNA editing efficiency in human liver2025 Scientific Reports article Biochemistry, Genetics and Molecular Biology RNA regulation and disease Open access
Mònica Aguilà, Nicole H.P. Cnubben, David A. Parfitt, Bruno Albuquerque, Peter C. de Visser, Marlieke Molendijk, +1 more
1citations -
Prevalence and determinants of over- and undertreatment among users of antihypertensive drugs in the general population: the Rhineland Study2023 European Journal of Preventive Cardiology article Medicine Blood Pressure and Hypertension Studies Open access
Nersi Alaeddin, Gökhan Pehlivan, Monique M.B. Breteler, Folgerdiena M. de Vries
1citations -
P-802 TFAP2C is required for proper segregation of developmental markers regulating trophectoderm commitment during mouse preimplantation development2023 Human Reproduction conference-abstract Biochemistry, Genetics and Molecular Biology Developmental Biology and Gene Regulation Open access
Gwenny Cosemans, Annekatrien Boel, Bieke Bekaert, Dominic Stoop, Susana M. Chuva de Sousa Lopes, Paul J. Coucke, +3 more
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Review of A revolution in fragments. Traversing scales of justice, ideology and practice in Bolivia0citations
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O-099 TEAD4 regulates trophectoderm differentiation upstream of CDX2 in human preimplantation embryos2021 Human Reproduction conference-abstract Biochemistry, Genetics and Molecular Biology Developmental Biology and Gene Regulation
Panagiotis Stamatiadis, Annekatrien Boel, Gwenny Cosemans, Filip Van Nieuwerburgh, Björn Menten, Petra De Sutter, +3 more
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Production and Storage of High-Capacity Adenoviral Vectors for the Delivery of Advanced CRISPR Systems2026 Methods in molecular biology book-chapter Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access
Xiaoling Wang, Jin Liu, Josephine M. Janssen, Manuel A.F.V. Gonçalves
0citations -
Protocol for non-viral HDR-based CRISPR/Cas9 platform for small custom editing in primary T cells2026 Frontiers in Genome Editing article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access
Katariina Mamia, Anniken Solveig Matheson Sollano, Vanja Lundberg, Svetlana Vakkilainen, Eliisa Kekäläinen, Camilla Schalin-Jäntti, +6 more
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CRISPR-Cas9 induces large structural variants at on-target and off-target sites in vivo that segregate across generations2022 Nature Communications article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 1 patent
Ida Höijer, Anastasia Emmanouilidou, Rebecka Östlund, Robin van Schendel, Selma Bozorgpana, Marcel Tijsterman, +4 more
196citations -
Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome2021 EMBO Molecular Medicine article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 7 patents
Valentina Vavassori, Elisabetta Mercuri, Genni Enza Marcovecchio, Maria Carmina Castiello, Giulia Schiroli, Luisa Albano, +17 more
53citations -
PLGA-Nanoparticles for Intracellular Delivery of the CRISPR-Complex to Elevate Fetal Globin Expression in Erythroid Cells2020 Biomaterials article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access cited by 1 patent
Luis Javier Cruz, Thamar van Dijk, Olena Vepris, Tracy M.W.Y. Li, Timo Schomann, Fabio Baldazzi, +5 more
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