January 01, 2015 article Open access Off-target Effects in CRISPR/Cas9-mediated Genome Engineering Molecular Therapy — Nucleic Acids DOI: 10.1038/mtna.2015.37 Full text (OA) OpenAlex Authors 0 Author list not loaded yet. Cited by 7 stored of 1,326 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Gene therapy strategies for RAG1 deficiency: Challenges and breakthroughs 2024 Immunology Letters article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access 8 citations A comprehensive overview of CRISPR/Cas 9 technology and application thereof in drug discovery 2022 Journal of Cellular Biochemistry article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access 22 citations CRISPR applications for Duchenne muscular dystrophy: From animal models to potential therapies 2022 WIREs Mechanisms of Disease article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access cited by 1 patent 23 citations A Small Key for a Heavy Door: Genetic Therapies for the Treatment of Hemoglobinopathies 2021 Frontiers in Genome Editing article Medicine Hemoglobinopathies and Related Disorders Open access cited by 4 patents 19 citations Developments in reading frame restoring therapy approaches for Duchenne muscular dystrophy 2020 Expert Opinion on Biological Therapy article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 25 citations CRISPR/Cas with ribonucleoprotein complexes and transiently selected telomere vectors allows highly efficient marker-free and multiple genome editing in Botrytis cinerea 2020 PLoS Pathogens article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 1 patent 128 citations Meeting a Challenge: A View on Studying Transcriptional Control of Genes Involved in Plant Biomass Degradation in Aspergillus niger 2020 Grand challenges in biology and biotechnology book-chapter Biochemistry, Genetics and Molecular Biology Fungal and yeast genetics research 2 citations 7 results References 0