Gene therapy returns to centre stage

• EMA commentary on the guideline on quality, nonclinical and clinical aspects of medicinal products containing genetically modified cells

  2024 British Journal of Clinical Pharmacology article Medicine Biomedical Ethics and Regulation Open access

  11

  citations
• Nucleic acid degradation as barrier to gene delivery: a guide to understand and overcome nuclease activity

  2023 Chemical Society Reviews review Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery cited by 1 patent

  129

  citations
• The quest for the holy grail: overcoming challenges in expanding human hematopoietic stem cells for clinical use

  2023 Stem Cell Investigation article Medicine Hematopoietic Stem Cell Transplantation Open access cited by 1 patent

  27

  citations
• Cellular uptake of modified mRNA occurs via caveolae-mediated endocytosis, yielding high protein expression in slow-dividing cells

  2023 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access

  19

  citations
• Efficient mRNA delivery using lipid nanoparticles modified with fusogenic coiled-coil peptides

  2023 Nanoscale article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery

  22

  citations
• Precision Medicine Using Pharmacogenomic Panel-Testing

  2022 Clinics in Laboratory Medicine article Pharmacology, Toxicology and Pharmaceutics Pharmacogenetics and Drug Metabolism

  3

  citations
• Precision Medicine Using Pharmacogenomic Panel-Testing

  2020 Advances in Molecular Pathology article Pharmacology, Toxicology and Pharmaceutics Pharmacogenetics and Drug Metabolism Open access

  2

  citations

7 results