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Expression-based selection identifies a microglia-tropic AAV capsid for direct and CSF routes of administration in mice2024 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 1 patent
Miguel C. Santoscoy, Paula Espinoza, Killian S. Hanlon, Lisa Nieland, Carrie Ng, Christian Elias Badr, +7 more
2citations -
mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy2023 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 5 patents
Lisa Maria Riedmayr, Klara Sonnie Hinrichsmeyer, Stefan Bernhard Thalhammer, Nina Karguth, Sybille Böhm, David Manuel Mittas, +11 more
1citations -
USH2A High-Capacity Adenoviral Vector Restores usherin, whirlin, and ADGRV1 in Photoreceptor Cells of Retinal Organoids2026 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access
Rossella Valenzano, Xuefei Lu, Aat A. Mulder, Elon H C van Dijk, Roman I. Koning, Manuel A.F.V. Gonçalves, +1 more
0citations -
Genome-enabled insights into the biology of thrips as crop pests2020 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Insect Resistance and Genetics Open access
Dorith Rotenberg, Aaron A. Baumann, Sulley K. Ben-Mahmoud, Olivier Christiaens, Wannes Dermauw, Panagiotis Ioannidis, +50 more
15citations -
Intratumoral gene delivery of 4-1BBL boosts IL-12-triggered anti-glioblastoma immunity2025 bioRxiv (Cold Spring Harbor Laboratory) preprint Medicine Glioma Diagnosis and Treatment Open access
Taral R. Lunavat, Lisa Nieland, Sanne M. van de Looij, Alexandra J E M de Reus, Charles Couturier, Chadi A. El Farran, +18 more
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KIF23 regulation by miR-107 controls replicative tumor cell fitness in mouse and human hepatocellular carcinoma2023 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology MicroRNA in disease regulation Open access
Sanchari Roy, Carolin Lohr, Rossella Pellegrino, Mihael Vucur, Michael T. Singer, Veronika Buettner, +7 more
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Gene Supplementation of MYO7A or activation of Myo7b for treatment of Usher syndrome 1B2026 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access
David Manuel Mittas, Dina Yehia Otify, Zoran Gavrilov, Thomas Heigl, Jan Suchomski, Paulina Deltuvaite, +27 more
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Distinct roles of IDR and CCD domains control PABPN1 aggregation and enable therapeutic rescue2026 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology RNA Research and Splicing Open access
Milad Shademan, Iolanda Vendrell, Alberto Malerba, s Khoshbash, Sarah Flannery, March, +4 more
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Mono-ADP-ribosylation by ARTD10 restricts Chikungunya virus replication by interfering with the proteolytic activity of nsP22020 bioRxiv (Cold Spring Harbor Laboratory) preprint Immunology and Microbiology interferon and immune responses Open access
Sarah Krieg, Fabian Pott, Laura Eckei, Maud Verheirstraeten, Mareike Bütepage, Barbara E. Lippok, +3 more
10citations -
Immunogenicity of an Ad26-based SARS-CoV-2 Omicron Vaccine in Naïve Mice and SARS-CoV-2 Spike Pre-immune Hamsters2022 bioRxiv (Cold Spring Harbor Laboratory) preprint Medicine SARS-CoV-2 and COVID-19 Research Open access cited by 1 patent
Maarten Swart, Adriaan de Wilde, Sonja P. R. Schmit-Tillemans, Johan W. A. Verspuij, Chenandly Daal, Ying Choi, +15 more
2citations -
Roles for the long non-coding RNA Pax6os1 / PAX6-AS1 in pancreatic beta cell identity and function2020 bioRxiv (Cold Spring Harbor Laboratory) preprint Medicine Pancreatic function and diabetes Open access
Livia López–Noriega, Rebecca Callingham, Aida Martínez-Sánchez, Sameena Nawaz, Grazia Pizza, Nejc Haberman, +13 more
6citations -
AAV6-HCN4t-mediated biological pacing as a potential life-saving therapy for congenital complete heart block2025 bioRxiv (Cold Spring Harbor Laboratory) preprint Medicine Cardiac electrophysiology and arrhythmias Open access
Jianan Wang, Evelien E. Birza, Veronique M.F. Meijborg, Arie O. Verkerk, Aina Cervera-Barea, Timo Jonker, +20 more
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Low-Dose Ad26.COV2.S Protection Against SARS-CoV-2 Challenge in Rhesus Macaques2021 bioRxiv (Cold Spring Harbor Laboratory) preprint Medicine SARS-CoV-2 and COVID-19 Research Open access
Xuan He, Abishek Chandrashekar, Roland C. Zahn, Frank Wegmann, Jingyou Yu, Noe B. Mercado, +26 more
13citations