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Partial correction of immunodeficiency by lentiviral vector gene therapy in mouse models carrying Rag1 hypomorphic mutations2023 Frontiers in Immunology article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 1 patent
Maria Carmina Castiello, Martina Di Verniere, Elena Fontana, Sara Penna, Lucia Piceni Sereni, Alessandra Zecchillo, +12 more
4citations -
Isolation, Culture, and Genetic Engineering of Mammalian Primary Pigment Epithelial Cells for Non-Viral Gene Therapy2021 Journal of Visualized Experiments article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders
Thais Bascuas, Martina Kropp, Nina Harmening, Brittany M. Wong, Sandra Johnen, Zsuzsanna Izsvák, +1 more
2citations -
Isolation, Culture, and Genetic Engineering of Mammalian Primary Pigment Epithelial Cells for Non-Viral Gene Therapy2021 Journal of Visualized Experiments article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders
Thais Bascuas, Martina Kropp, Nina Harmening, Brittany M. Wong, Sandra Johnen, Zsuzsanna Izsvák, +1 more
0citations -
Bi-allelic variants in CELSR3 are implicated in central nervous system and urinary tract anomalies2024 npj Genomic Medicine article Biochemistry, Genetics and Molecular Biology Genetic and Kidney Cyst Diseases Open access
Jil D. Stegmann, Jeshurun C. Kalanithy, Gabriel C. Dworschak, Nina Ishorst, Enrico Mingardo, Filipa M. Lopes, +64 more
4citations -
The EHA Research Roadmap: Hematopoietic Stem Cells and Allotransplantation.2022 Apollo (University of Cambridge) other Medicine Hematopoietic Stem Cell Transplantation Open access
Willem E. Fibbe, Rosa Bernardi, Pierre Charbord, Daniela S. Krause, Cristina Lo Celso, Simón Méndez‐Ferrer, +6 more
1citations -
Generation, functional analysis and applications of isogenic three-dimensional self-aggregating cardiac microtissues from human pluripotent stem cells2021 Nature Protocols article Biochemistry, Genetics and Molecular Biology Pluripotent Stem Cells Research Open access cited by 12 patents
Giulia Campostrini, Viviana Meraviglia, Elisa Giacomelli, Ruben W.J. van Helden, Loukia Yiangou, Richard P. Davis, +3 more
109citations