-
sncRNA levels predict SNORD105B is a novel biomarker of chronic kidney disease risk and SGLT2 inhibitor response in type 2 diabetes2026 Molecular Therapy — Nucleic Acids article Medicine Chronic Kidney Disease and Diabetes Open access
Juliette A. de Klerk, Roderick C. Slieker, Joline W. J. Beulens, Janneke H D Peerlings, Hailiang Mei, Petra J. M. Elders, +4 more
2citations -
Using muscle homing peptide CyPep10 to deliver phosphorodiamidate morpholino oligomers in the mdx mouse2025 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access
Anne-Fleur E. Schneider, Christa L. Tanganyika-de Winter, Silvana M.G. Jirka, Xuyu Tan, Emily G. Thompson, Kristen Ha, +4 more
1citations -
Effect of degeneration stage on non-viral tissue transfection of rd10 retina ex vivo2025 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access
Corinne Marie, Zsuzsanna Izsvák, Frank Ulrich Müller, Gabriele Thumann, Peter Walter, Sandra Johnen
0citations -
Targeting liver angiotensinogen with siRNA enhances podocyte regeneration through renin lineage cells in experimental kidney disease2026 Molecular Therapy — Nucleic Acids article Medicine Renin-Angiotensin System Studies Open access
Loïs A.K. van der Pluijm, Angela Koudijs, A.H. Jan Danser, Joris I. Rotmans, Roel Bijkerk
0citations -
Y-RNAs and their fragments reflect kidney injury in diabetic kidney disease2026 Molecular Therapy — Nucleic Acids article Medicine Chronic Kidney Disease and Diabetes Open access
Zhao Qiao, Yunyi Liang, Rudmer J. Postma, Jacques M.G.J. Duijs, Juliette A. de Klerk, Leen M. ‘t Hart, +3 more
0citations -
Timing matters: Exon skipping therapy is most effective when initiated early in a mouse model of Duchenne muscular dystrophy2026 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access
Sofia Stenler, Junyu Huang, Tirsa L.E. van Westering, Anna M. L. Coenen-Stass, Yahya E. Jad, Kaarel Krjutškov, +3 more
0citations -
Givinostat enhances antisense oligonucleotide efficacy in the mdx52 model of Duchenne muscular dystrophy2026 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access
Xaysongkhame Phongsavanh, Cécile Gastaldi, Astrid Mottais, Mathilde Doisy, Olivier Le Coz, Sandra de Haan, +3 more
0citations -
Safety and toxicity assessment of antisense oligonucleotides in brain-relevant human cellular models2026 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access
Laura Colar Zanjko, Raúl Andrés-Santamaria, Willeke M.C. van Roon-Mom, András Dinnyés
0citations