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Fatigue and health‐related quality of life in paroxysmal nocturnal haemoglobinuria: A post hoc analysis of the pegcetacoplan PEGASUS trial data2023 European Journal Of Haematology article Immunology and Microbiology Complement system in diseases Open access
Jens Panse, Koo Wilson, Jesse Fishman, Piotr Wojciechowski, Marlena Wdowiak, Regina Horneff, +3 more
6citations -
RESULTS OF THE PEGASUS PHASE 3 RANDOMIZED TRIAL DEMONSTRATING SUPERIORITY OF THE C3 INHIBITOR PEGCETACOPLAN COMPARED TO ECULIZUMAB IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA2020 Hematology Transfusion and Cell Therapy article Immunology and Microbiology Complement system in diseases Open access
Peter Hillmen, Jeff Szer, Britta Höchsmann, Jens Panse, Jean‐Jacques Kiladjian, Carlos M. DeCastro, +7 more
3citations -
MDS-112 Normalization of Hematologic and Health-Related Quality of Life Markers in Patients With Paroxysmal Nocturnal Hemoglobinuria Treated With Pegcetacoplan and Baseline Hemoglobin at or Above 10 g/dL2022 Clinical Lymphoma Myeloma & Leukemia conference-abstract Immunology and Microbiology Complement system in diseases
Dharmik Desai, Jens Panse, Nicolas Daguindau, Sonia Okuyama, Régis Peffault de Latour, Philippe Schafhausen, +5 more
1citations -
MDS-1159: Long-Term Safety With Iptacopan Treatment in Patients With Paroxysmal Nocturnal Hemoglobinuria: Pooled Analysis of Data From Phase 2 and 3 Studies and the Roll-Over Extension Program2026 Clinical Lymphoma Myeloma & Leukemia conference-abstract Immunology and Microbiology Complement system in diseases
Alexander Röth, Austin Gladston Kulasekararaj, Camilla Frieri, Flore Sicre de Fontbrune, Phillip Scheinberg, Bor‐Sheng Ko, +8 more
0citations -
Phase III Randomized COMMODORE 1 Trial: 2-Year Safety and Efficacy of Crovalimab in Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) Who Switched from Eculizumab2024 Blood conference-abstract Immunology and Microbiology Complement system in diseases Open access
Phillip Scheinberg, Diego V. Clé, Bérangère Devalet, Valentina Giai, Cristina Barrenetxea Lekue, Hsuan‐Yu Lin, +12 more
0citations -
Poster: MDS-112 Normalization of Hematologic and Health-Related Quality of Life Markers in Patients With Paroxysmal Nocturnal Hemoglobinuria Treated With Pegcetacoplan and Baseline Hemoglobin at or Above 10 g/dL2022 Clinical Lymphoma Myeloma & Leukemia article Immunology and Microbiology Complement system in diseases
Dharmik Desai, Jens Panse, Nicolas Daguindau, Sonia Okuyama, Régis Peffault de Latour, Philippe Schafhausen, +5 more
0citations -
POSTER: MDS-1167: Long-Term Hematologic Control and Safety in Patients With Paroxysmal Nocturnal Hemoglobinuria Treated With Iptacopan: Six-Year Follow-Up From Phase 2 Studies and Roll-Over Extension Program2026 Clinical Lymphoma Myeloma & Leukemia article Immunology and Microbiology Complement system in diseases
Antonio Maria Risitano, Camilla Frieri, Bor‐Sheng Ko, Lily Wong Lee Lee, Alexander Röth, Flore Sicre de Fontbrune, +8 more
0citations -
POSTER: MDS-1159: Long-Term Safety With Iptacopan Treatment in Patients With Paroxysmal Nocturnal Hemoglobinuria: Pooled Analysis of Data From Phase 2 and 3 Studies and the Roll-Over Extension Program2026 Clinical Lymphoma Myeloma & Leukemia article Immunology and Microbiology Complement system in diseases
Alexander Röth, Austin GKulasekararaj, Camilla Frieri, Flore Sicre de Fontbrune, Phillip Scheinberg, Bor‐Sheng Ko, +8 more
0citations -
WCN26-5461 ORAL IPTACOPAN THERAPY IN C3 GLOMERULOPATHY SHOWS CONSISTENT STABILIZATION OF eGFR SLOPE ACROSS PATIENT SUBGROUPS2026 Kidney International Reports article Immunology and Microbiology Complement system in diseases Open access
Andrew S. Bomback, Carla Nester, Richard J.H. Smith, Liz Lightstone, Marina Vivarelli, Sophie Chauvet, +7 more
0citations -
Poster: MDS-134: Efficacy and Safety at 48 Weeks of Pegcetacoplan in Adult Paroxysmal Nocturnal Hemoglobinuria Patients with Suboptimal Response to Prior Eculizumab Treatment2021 Clinical Lymphoma Myeloma & Leukemia article Immunology and Microbiology Complement system in diseases
Ilene Ceil Weitz, Régis Peffault de Latour, Jeff Szer, Alexander Röth, Britta Höchsmann, Jens Panse, +12 more
0citations -
Essai de phase III randomisé, multicentrique et en ouvert COMMODORE 1 : comparaison du crovalimab et de l’éculizumab chez des patients atteints d’hémoglobinurie paroxystique nocturne (HPN) déjà traités par un inhibiteur du complément
C. Tessier, Louis Terriou, Phillip Scheinberg, Diego V. Clé, Valentina Giai, M. Hus, +10 more
0citations -
POSTER: MDS-273 Oral Iptacopan Monotherapy Increases Paroxysmal Nocturnal Hemoglobinuria (PNH) Red Blood Cell Clone Size Via Control of Intra- and Extravascular Hemolysis in Anti-C5-Treated PNH Patients With Anemia2023 Clinical Lymphoma Myeloma & Leukemia article Immunology and Microbiology Complement system in diseases
Antonio Maria Risitano, Alexander Röth, Austin Gladston Kulasekararaj, Phillip Scheinberg, Eros Di Bona, Morag Griffin, +27 more
0citations -
monarch-initiative/mondo: v2026-02-032026 Zenodo (CERN European Organization for Nuclear Research) software Biochemistry, Genetics and Molecular Biology Biomedical Text Mining and Ontologies Open access
Nicole Vasilevsky, Chris J Mungall, Nicolas Matentzoglu, Sabrina Toro, Trish Whetzel, MeeSiing Ngu, +21 more
0citations -
Combined C5 and CD14 inhibition balances immunological miRNA responses after multiple trauma in pigs2025 DataverseNL dataset Immunology and Microbiology Inflammation biomarkers and pathways Open access
Rald V. M. Groven, Ümit Mert, Johannes Greven, Zhizhen He, Nan Zhou, Martijn Poeze, +5 more
0citations -
Antifouling Surface‐Attached Hydrogel Nanocoatings Redefined: Green Solvent‐Based, Degradable, and High‐Performance Protection Against Foulants2025 Advanced Materials Interfaces article Materials Science Polymer Surface Interaction Studies Open access
Jenny Englert, Marc Palà, Jonas Quandt, Hannah Sieben, Oliver Grottke, Gerard Lligadas, +1 more
1citations -
POS0253 DIFFERENCES IN THE EFFECT OF C4A and C4B COPY NUMBERS ON SSc SEROLOGICAL AND CLINICAL SUBTYPES2025 Annals of the Rheumatic Diseases article Medicine Systemic Sclerosis and Related Diseases Open access
Joaquín Martínez‐López, Carlos Rangel‐Peláez, Inmaculada Rodriguez‐Martin, Alfredo Guillén del Castillo, Carmen Pilar Simeón‐Aznar, José Luís Callejas-Rubio, +14 more
0citations -
The future role of thermal energy storage in 100% renewable electricity systems2023 Renewable and Sustainable Energy Transition article Engineering Integrated Energy Systems Optimization Open access
Rhys Jacob, Maximilian Hoffmann, Jann Michael Weinand, Jochen Linßen, Detlef Stolten, Michael Rolf Müller
24citations