Papers matching “clinical trials” in Statistical Methods in Clinical Trials 182
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Expert consensus recommendations on the use of randomized clinical trials for drug approval in psychiatry- comparing trial designs2022 European Neuropsychopharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Miriam von Mücke Similon, Cecilia Paasche, Fas J. Krol, Bernard Lerer, Guy M. Goodwin, Michael Berk, +34 more
16citations -
Multi-stakeholder sessions on major innovation topics in rare disease clinical trials2024 Orphanet Journal of Rare Diseases article Mathematics Statistical Methods in Clinical Trials Open access
Daniel Bodden, Stefanie Schoenen, Stephanie Wied, Johan Verbeeck, Maya Dirani, Nicole Maria Heussen, +3 more
3citations -
Istore: a project on innovative statistical methodologies to improve rare diseases clinical trials in limited populations2024 Orphanet Journal of Rare Diseases article Mathematics Statistical Methods in Clinical Trials Open access
Stefanie Schoenen, Johan Verbeeck, Lukas Koletzko, Isabella Brambilla, Mathieu Kuchenbuch, Maya Dirani, +5 more
6citations -
A first step towards best practice recommendations for the design and statistical analyses of pragmatic clinical trials: A modified Delphi approach2022 British Journal of Clinical Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Victoria Palin, Tjeerd Pieter van Staa, Stephanie Steels, Andrea B. Troxel, Rolf H. H. Groenwold, Thomas MacLennan MacDonald, +7 more
6citations -
Pragmatic gynecologic cancer clinical trials: statements and roadmap from the Gynecologic Cancer InterGroup Chicago Brainstorming Meeting2026 International Journal of Gynecological Cancer article Mathematics Statistical Methods in Clinical Trials Open access
Ainhoa Madariaga, Ana Veneziani, Michael A. Bookman, Nicholas Counsell, Austin Miller, John Andrews, +24 more
0citations -
Sentinel dosing: A proposed algorithm to guide decision making on which cohorts in early phase clinical pharmacology trials should use this approach2025 British Journal of Clinical Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Jules A. A. C. Heuberger, Perry de Jongh, Ewoud‐Jan van Hoogdalem, Wim J. Tamminga, Pieter de Graeff, Geert Jan Groeneveld
4citations -
The impact of allocation bias on test decisions in clinical trials with multiple endpoints using multiple testing strategies2024 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Stefanie Schoenen, Nicole Maria Heussen, Johan Verbeeck, R.-D Hilgers
6citations -
Procedure for pooling clinical outcome data from DRUP-like clinical trials using the OMOP model.2025 Journal of Clinical Oncology conference-abstract Mathematics Statistical Methods in Clinical Trials
T.M. Kringelbach, Gro Live Fagereng, Gabriel Bratseth Stav, Maria Martin Agudo, Soemeya F. Haj Mohammad, Florentine A.J. Verbeek, +13 more
0citations -
Accelerating vaccine trial conduct in a pandemic with a hot spot‐based inclusion strategy using trial and epidemic simulation2021 Clinical and Translational Science article Mathematics Statistical Methods in Clinical Trials Open access
Johan L. van der Plas, Michiel Joost van Esdonk, Ingrid M. C. Kamerling, Adam F. Cohen
7citations