Innovative methodologies for rare diseases clinical trials

Orphanet Journal of Rare Diseases, vol. 19, pp. 190

Authors 2

1. Rima Nabbout corresponding

   Inserm · Assistance Publique – Hôpitaux de Paris · Université Paris Cité · Hôpital Necker-Enfants Malades · Institut des Maladies Génétiques Imagine

   Affiliation as printed

   Assistance Publique-Hôpitaux de Paris, Hôpital Necker-Enfants Malades, Paris, France. rima.nabbout@aphp.fr

   Institut Imagine, INSERM U1163, Paris, France. rima.nabbout@aphp.fr

   Reference centre for rare epilepsies Université Paris cité, Paris, France. rima.nabbout@aphp.fr

   Reference centre for rare epilepsies Université Paris cité, Paris, France

2. R.-D Hilgers corresponding Aachen Institute of Medical Statistics

   RWTH Aachen University

   Affiliation as printed

   RWTH Aachen University, Institute of Medical Statistics, 52074, Aachen, Germany. rhilgers@ukaachen.de

   RWTH Aachen University, Institute of Medical Statistics, 52074, Aachen, Germany