-
Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations2021 Molecular Therapy article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access cited by 8 patents
Kalyan Dulla, Ralph W. N. Slijkerman, Hester C. van Diepen, Sílvia Albert, Margo Dona, Wouter Beumer, +19 more
148citations -
Predicting genotoxicity of viral vectors for stem cell gene therapy using gene expression-based machine learning2021 Molecular Therapy article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 1 patent
Adrian Schwarzer, Steven Roger Talbot, Anton Selich, Michael Alexander Morgan, Juliane Wilhelmine Schott, Oliver Dittrich‐Breiholz, +11 more
51citations -
Intratumoral delivery of 4-1BBL boosts IL-12-triggered anti-glioma immunity2025 Molecular Therapy article Medicine Glioma Diagnosis and Treatment Open access cited by 1 patent
Taral R. Lunavat, Lisa Nieland, Sanne M. van de Looij, Alexandra J E M de Reus, Charles Couturier, Chadi A. El Farran, +18 more
6citations
4 results