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Istore: a project on innovative statistical methodologies to improve rare diseases clinical trials in limited populations2024 Orphanet Journal of Rare Diseases article Mathematics Statistical Methods in Clinical Trials Open access
Stefanie Schoenen, Johan Verbeeck, Lukas Koletzko, Isabella Brambilla, Mathieu Kuchenbuch, Maya Dirani, +5 more
6citations -
Clarifying the biological and statistical assumptions of cross-sectional biological age predictors: an elaborate illustration using synthetic and real data2024 BMC Medical Research Methodology article Mathematics Statistical Methods in Epidemiology Open access cited by 1 patent
Marije H. Sluiskes, Jelle J. Goeman, Marian Beekman, P. Eline Slagboom, Hein Putter, Mar Rodríguez‐Girondo
38citations -
A Knowledge Base of Designs and Statistical Methods for Adaptive Clinical Dose‐Finding Trials2026 Pharmaceutical Statistics review Mathematics Statistical Methods in Clinical Trials Open access
Rob Kessels, Yongxi Long, René Spijker, Ewoud Schuit, Marieke J Hollestelle, Chris van Lieshout, +3 more
0citations -
Quality Tolerance Limits’ Place in the Quality Management System and Link to the Statistical Trial Design: Case Studies and Recommendations from Early Adopters2023 Therapeutic Innovation & Regulatory Science article Mathematics Statistical Methods in Clinical Trials Open access
Marion Wolfs, Łukasz Bojarski, Lynne Cesario, Marcin Makowski, Linda B. Sullivan
8citations -
Predictive averaging and Rubin’s rule-based model pooling to predict survival risk with imputations in the presence of missing patient data: methodology and verification using two case studies and simulations2026 BMC Medical Research Methodology article Mathematics Statistical Methods and Bayesian Inference Open access
Bart J.A. Mertens, Lars L. J. van der Burg, Erwan Donal, Nina Ajmone Marsan, Liesbeth C. de Wreede
1citations -
Ordinal outcome analysis improves the detection of between-hospital differences in outcome2021 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Iris E. Ceyisakar, Nikki van Leeuwen, Diederik W.J. Dippel, Ewout Willem Steyerberg, Hester Floor Lingsma
23citations -
Methodological guidance for the evaluation and updating of clinical prediction models: a systematic review2022 BMC Medical Research Methodology review Mathematics Statistical Methods in Epidemiology Open access
Mary Ann E. Binuya, Ellen G. Engelhardt, Winnie Schats, Marjanka K. Schmidt, Ewout Willem Steyerberg
233citations