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A Pharmacometrics‐Informed Trial Simulation Framework for Optimizing Study Designs for Disease‐Modifying Treatments in Rare Neurological Disorders2025 CPT Pharmacometrics & Systems Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Yevgen V. Ryeznik, R.-D Hilgers, Nicole Maria Heussen, Emmanuelle Comets, France Mentré, Niels Hendrickx, +7 more
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Drug exposure misclassification in pharmacoepidemiology: Sources and relative impact2021 Pharmacoepidemiology and Drug Safety article Mathematics Statistical Methods in Epidemiology Open access
Mirjam Hempenius, Rolf H. H. Groenwold, Anthonius de Boer, Olaf H. Klungel, Helga Gardarsdóttir
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