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A first step towards best practice recommendations for the design and statistical analyses of pragmatic clinical trials: A modified Delphi approach2022 British Journal of Clinical Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Victoria Palin, Tjeerd Pieter van Staa, Stephanie Steels, Andrea B. Troxel, Rolf H. H. Groenwold, Thomas MacLennan MacDonald, +7 more
6citations -
Crowdsourcing multiverse analyses to explore the impact of different data-processing and analysis decisions: A tutorial.2025 Psychological Methods article Mathematics Statistical Methods and Bayesian Inference Open access
Tom Heyman, Ekaterina Pronizius, Savannah C Lewis, Oguz Ali Acar, Matus Adamkovic, Ettore Ambrosini, +57 more
2citations -
Pragmatic gynecologic cancer clinical trials: statements and roadmap from the Gynecologic Cancer InterGroup Chicago Brainstorming Meeting2026 International Journal of Gynecological Cancer article Mathematics Statistical Methods in Clinical Trials Open access
Ainhoa Madariaga, Ana Veneziani, Michael A. Bookman, Nicholas Counsell, Austin Miller, John Andrews, +24 more
0citations -
Lessons learnt when accounting for competing events in the external validation of time-to-event prognostic models2021 International Journal of Epidemiology article Mathematics Statistical Methods in Epidemiology Open access
Chava L. Ramspek, Lucy Teece, Kym I E Snell, Marie Evans, Richard D Riley, Maarten van Smeden, +2 more
45citations -
A Pharmacometrics‐Informed Trial Simulation Framework for Optimizing Study Designs for Disease‐Modifying Treatments in Rare Neurological Disorders2025 CPT Pharmacometrics & Systems Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Yevgen V. Ryeznik, R.-D Hilgers, Nicole Maria Heussen, Emmanuelle Comets, France Mentré, Niels Hendrickx, +7 more
3citations -
Maximizing Treatment Opportunities: Assessing Protocol Waivers’ Impact on Safety and Outcome in the Drug Rediscovery Protocol2024 Clinical Cancer Research article Mathematics Statistical Methods in Clinical Trials Open access
Jade M. van Berge Henegouwen, Laurien Joanna Zeverijn, Birgit S. Geurts, Louisa Rose Hoes, Hanneke van der Wijngaart, Vincent van der Noort, +7 more
2citations -
Patient preference trials in oncology: a scoping review and recommendations on reporting2025 Journal of Clinical Epidemiology article Mathematics Statistical Methods in Clinical Trials Open access
Denice Kamp, Roy P. C. Kessels, Nadia Haj Mohammad, Renée Schmitz, Joanna IntHout, Hanneke W.M. van Laarhoven, +2 more
2citations
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