July 08, 2026 article Open access Alternative conditioning regimens for hemoglobinopathy gene therapy: balancing efficacy, toxicity, and the next frontier Blood Advances DOI: 10.1182/bloodadvances.2026019856 Full text (OA) OpenAlex Authors 0 Author list not loaded yet. Cited by 0 stored of 0 References 5 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Targeted busulfan-based reduced-intensity conditioning and HLA-matched HSCT cure hemophagocytic lymphohistiocytosis 2020 Blood Advances article Medicine Autoimmune and Inflammatory Disorders Research Open access 53 citations Busulfan–fludarabine- or treosulfan–fludarabine-based myeloablative conditioning for children with thalassemia major 2022 Annals of Hematology article Medicine Hematopoietic Stem Cell Transplantation 35 citations Association of busulfan exposure and outcomes after HCT for patients with an inborn error of immunity 2024 Blood Advances article Immunology and Microbiology Immunodeficiency and Autoimmune Disorders Open access 19 citations Busulfan Interlaboratory Proficiency Testing Program Revealed Worldwide Errors in Drug Quantitation and Dose Recommendations 2023 Therapeutic Drug Monitoring article Medicine Clinical Laboratory Practices and Quality Control Open access 13 citations Busulfan–fludarabine‐ or treosulfan–fludarabine‐based conditioning before allogeneic HSCT from matched sibling donors in paediatric patients with sickle cell disease: A study on behalf of the EBMT Paediatric Diseases and Inborn Errors Working Parties 2023 British Journal of Haematology article Medicine Hematopoietic Stem Cell Transplantation 8 citations 5 results