Engineered CRISPR-Cas9 nucleases with altered PAM specificities

• One-step generation of tumor models by base editor multiplexing in adult stem cell-derived organoids

  2023 Nature Communications article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 1 patent

  65

  citations
• Prime editing: advances and therapeutic applications

  2023 Trends in biotechnology review Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 10 patents

  199

  citations
• Nanomedicine for Treating Muscle Dystrophies: Opportunities, Challenges, and Future Perspectives

  2022 International Journal of Molecular Sciences article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access

  19

  citations
• CRISPR applications for Duchenne muscular dystrophy: From animal models to potential therapies

  2022 WIREs Mechanisms of Disease article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access cited by 1 patent

  23

  citations
• Establishment of human fetal hepatocyte organoids and CRISPR–Cas9-based gene knockin and knockout in organoid cultures from human liver

  2020 Nature Protocols article Medicine Liver physiology and pathology Open access cited by 1 patent

  159

  citations
• Human sensory neurons derived from pluripotent stem cells for disease modelling and personalized medicine

  2020 Neurobiology of Pain article Biochemistry, Genetics and Molecular Biology Pluripotent Stem Cells Research Open access

  56

  citations
• Integrating gene delivery and gene-editing technologies by adenoviral vector transfer of optimized CRISPR-Cas9 components

  2020 Gene Therapy article Biochemistry, Genetics and Molecular Biology CRISPR and Genetic Engineering Open access cited by 1 patent

  66

  citations

7 results