Precise RNA editing by recruiting endogenous ADARs with antisense oligonucleotides

• RNA-based therapeutic opportunities for the treatment of kidney diseases

  2025 Nature Reviews Nephrology review Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery

  8

  citations
• Recommendations for detection, validation, and evaluation of RNA editing events in cardiovascular and neurological/neurodegenerative diseases

  2023 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology RNA regulation and disease Open access

  21

  citations
• Pediatric and Adult Liver Disease in Alpha-1 Antitrypsin Deficiency

  2023 Seminars in Liver Disease article Medicine Pediatric Hepatobiliary Diseases and Treatments

  15

  citations
• The epitranscriptome: RNA modifications in vascular remodelling

  2022 Atherosclerosis article Biochemistry, Genetics and Molecular Biology RNA modifications and cancer Open access

  23

  citations
• From Antisense RNA to RNA Modification: Therapeutic Potential of RNA-Based Technologies

  2021 Biomedicines article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access cited by 3 patents

  81

  citations
• Rational Design of RNA Editing Guide Strands: Cytidine Analogs at the Orphan Position

  2021 Journal of the American Chemical Society article Biochemistry, Genetics and Molecular Biology RNA regulation and disease Open access cited by 27 patents

  32

  citations
• Targeted Pseudouridylation: A Novel Approach for Suppressing Nonsense Mutations in Disease Genes

  2021 SSRN Electronic Journal preprint Biochemistry, Genetics and Molecular Biology RNA Research and Splicing Open access

  0

  citations
• Suppression of Nonsense Mutations by New Emerging Technologies

  2020 International Journal of Molecular Sciences article Biochemistry, Genetics and Molecular Biology RNA Research and Splicing Open access

  67

  citations

8 results