January 01, 2016 article Open access Antisense Oligonucleotide-based Splice Correction for USH2A-associated Retinal Degeneration Caused by a Frequent Deep-intronic Mutation Molecular Therapy — Nucleic Acids DOI: 10.1038/mtna.2016.89 Full text (OA) OpenAlex Authors 0 Author list not loaded yet. Cited by 5 stored of 133 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Syndromic retinitis pigmentosa 2024 Progress in Retinal and Eye Research article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access 39 citations Joining forces to develop individualized antisense oligonucleotides for patients with brain or eye diseases: the example of the Dutch Center for RNA Therapeutics 2024 Therapeutic Advances in Rare Disease article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access 9 citations Antisense oligonucleotide therapy corrects splicing in the common Stargardt disease type 1-causing variant ABCA4 c.5461-10T>C 2023 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access 41 citations Antisense oligonucleotide therapy for the common Stargardt disease type 1-causing variant in ABCA4 2022 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access 1 citations Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations 2021 Molecular Therapy article Biochemistry, Genetics and Molecular Biology Retinal Development and Disorders Open access cited by 8 patents 148 citations 5 results References 0