August 23, 2013 article DMD transcript imbalance determines dystrophin levels The FASEB Journal DOI: 10.1096/fj.13-232025 OpenAlex Authors 0 Author list not loaded yet. Cited by 15 stored of 48 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Givinostat enhances antisense oligonucleotide efficacy in the mdx52 model of Duchenne muscular dystrophy 2026 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 0 citations Timing matters: Exon skipping therapy is most effective when initiated early in a mouse model of Duchenne muscular dystrophy 2026 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 0 citations Unraveling the spatial landscape of dystrophinopathies: a transcriptomic approach to Becker and Duchenne muscular dystrophies 2026 The Journal of Pathology article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 2 citations Timing matters: exon skipping therapy is most effective when initiated early in a mouse model of Duchenne muscular dystrophy 2025 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 0 citations The complexity of dystrophin transcription and processing: implications of transcript imbalance on dystrophin gene targeting strategies 2025 Neuromuscular Disorders article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 3 citations Regional Expression of Dystrophin Gene Transcripts and Proteins in the Mouse Brain 2025 Cells article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 4 citations Understanding Duchenne muscular dystrophy-associated brain pathology 2025 Disease Models & Mechanisms article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 2 citations Networking to Optimize Dmd exon 53 Skipping in the Brain of mdx52 Mouse Model 2023 Biomedicines article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 11 citations DMD antisense oligonucleotide mediated exon skipping efficiency correlates with flanking intron retention time and target position within the exon 2023 RNA Biology article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 2 citations Next Generation Exon 51 Skipping Antisense Oligonucleotides for Duchenne Muscular Dystrophy 2023 Nucleic Acid Therapeutics article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access cited by 1 patent 19 citations Histone deacetylase inhibitors improve antisense-mediated exon-skipping efficacy in mdx mice 2022 Molecular Therapy — Nucleic Acids article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 17 citations DMD antisense oligonucleotide mediated exon skipping efficiency is affected by flanking intron retention time and target position within the exon 2022 bioRxiv (Cold Spring Harbor Laboratory) preprint Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 0 citations Developments in reading frame restoring therapy approaches for Duchenne muscular dystrophy 2020 Expert Opinion on Biological Therapy article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 25 citations 249th ENMC International Workshop: The role of brain dystrophin in muscular dystrophy: Implications for clinical care and translational research, Hoofddorp, The Netherlands, November 29th–December 1st 2019 2020 Neuromuscular Disorders article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 32 citations Premature termination codons in the DMD gene cause reduced local mRNA synthesis 2020 Proceedings of the National Academy of Sciences article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access cited by 2 patents 80 citations 15 results References 0