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• ▲ Daniela C. F. Salvatori

  Utrecht University Biochemistry, Genetics and Molecular Biology
  3.06k

  citations

  29

  h-index

  10

  Aachen papers
• ▲ Saskia Maas

  Amsterdam University Medical Centers · Rijndam Revalidatiecentrum Biochemistry, Genetics and Molecular Biology
  1.05k

  citations

  15

  h-index

  1

  Aachen papers
• ▲ Sophie Gerhardt

  Reutlingen University Medicine
  257

  citations

  4

  h-index

  3

  Aachen papers

3 results

• Successful Preclinical Development of Gene Therapy for Recombinase-Activating Gene-1-Deficient SCID

  2020 Molecular Therapy — Methods & Clinical Development article Biochemistry, Genetics and Molecular Biology Virus-based gene therapy research Open access cited by 3 patents

  58

  citations
• Consequences of excessive glucosylsphingosine in glucocerebrosidase-deficient zebrafish.

  2022 Journal of Lipid Research article Medicine Lysosomal Storage Disorders Research Open access

  18

  citations

2 results