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Predictive approaches to heterogeneous treatment effects: a scoping review2020 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
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Real-world and natural history data for drug evaluation in Duchenne muscular dystrophy: suitability of the North Star Ambulatory Assessment for comparisons with external controls
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FDA-Industry Scientific Exchange on assessing quantitative systems pharmacology models in clinical drug development: a meeting report, summary of challenges/gaps, and future perspective
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Measuring the success of blinding in placebo-controlled trials: Should we be so quick to dismiss it?2021 Journal of Clinical Epidemiology article Mathematics Statistical Methods in Clinical Trials Open access
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Ordinal outcome analysis improves the detection of between-hospital differences in outcome2021 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
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Tell me what you want, what you really really want: Estimands in observational pharmacoepidemiologic comparative effectiveness and safety studies2023 Pharmacoepidemiology and Drug Safety article Mathematics Statistical Methods in Clinical Trials Open access
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