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A Pharmacometrics‐Informed Trial Simulation Framework for Optimizing Study Designs for Disease‐Modifying Treatments in Rare Neurological Disorders2025 CPT Pharmacometrics & Systems Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Yevgen V. Ryeznik, R.-D Hilgers, Nicole Maria Heussen, Emmanuelle Comets, France Mentré, Niels Hendrickx, +7 more
3citations -
Drug exposure misclassification in pharmacoepidemiology: Sources and relative impact2021 Pharmacoepidemiology and Drug Safety article Mathematics Statistical Methods in Epidemiology Open access
Mirjam Hempenius, Rolf H. H. Groenwold, Anthonius de Boer, Olaf H. Klungel, Helga Gardarsdóttir
36citations -
Automated causal inference in application to randomized controlled clinical trials2022 Nature Machine Intelligence article Mathematics Advanced Causal Inference Techniques Open access
Ji Q. Wu, Nanda Horeweg, Marco de Bruyn, Remi A. Nout, Ina Maria Jurgenliemk-Schulz, Ludy C.H.W. Lutgens, +7 more
18citations -
From Biological Mechanisms to Causal Inference: Quantitative Systems Pharmacology and Causal Frameworks in Drug Development2026 Clinical Pharmacology & Therapeutics article Mathematics Statistical Methods in Clinical Trials Open access
Thomas Klabunde, Ramon Hernandez Vecino, Piet H. van der Graaf, Tommaso Andreani
0citations
25 results