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A first step towards best practice recommendations for the design and statistical analyses of pragmatic clinical trials: A modified Delphi approach2022 British Journal of Clinical Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Victoria Palin, Tjeerd Pieter van Staa, Stephanie Steels, Andrea B. Troxel, Rolf H. H. Groenwold, Thomas MacLennan MacDonald, +7 more
6citations -
Randomization in the age of platform trials: unexplored challenges and some potential solutions2025 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Olga M. Kuznetsova, Jennifer Ross, Daniel Bodden, Freda Cooner, Jonathan Chipman, Peter Jacko, +7 more
3citations -
Natural Experiments: Missed Opportunities for Causal Inference in Psychology2024 Advances in Methods and Practices in Psychological Science article Mathematics Advanced Causal Inference Techniques Open access
Michael P. Grosz, Adam Ayaita, Ruben C. Arslan, Susanne Buecker, Tobias Ebert, Paul Hünermund, +4 more
39citations -
Patient preference trials in oncology: a scoping review and recommendations on reporting2025 Journal of Clinical Epidemiology article Mathematics Statistical Methods in Clinical Trials Open access
Denice Kamp, Nadia Haj Mohammad, Renée Schmitz, Joanna IntHout, Hanneke W.M. van Laarhoven, Anne Maria May, +1 more
2citations -
Tell me what you want, what you really really want: Estimands in observational pharmacoepidemiologic comparative effectiveness and safety studies2023 Pharmacoepidemiology and Drug Safety article Mathematics Statistical Methods in Clinical Trials Open access
Kim Luijken, Rik van EEKELEN, Helga Gardarsdóttir, Rolf H. H. Groenwold, Nan van Geloven
21citations -
The impact of allocation bias on test decisions in clinical trials with multiple endpoints using multiple testing strategies2024 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Stefanie Schoenen, Nicole Maria Heussen, Johan Verbeeck, R.-D Hilgers
6citations -
Pragmatic gynecologic cancer clinical trials: statements and roadmap from the Gynecologic Cancer InterGroup Chicago Brainstorming Meeting2026 International Journal of Gynecological Cancer article Mathematics Statistical Methods in Clinical Trials Open access
Ainhoa Madariaga, Ana Carolina Veneziani, Michael A. Bookman, Nicholas Counsell, Austin Miller, John Andrews, +24 more
0citations -
A Pharmacometrics‐Informed Trial Simulation Framework for Optimizing Study Designs for Disease‐Modifying Treatments in Rare Neurological Disorders2025 CPT Pharmacometrics & Systems Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Yevgen V. Ryeznik, R.-D Hilgers, Nicole Maria Heussen, Emmanuelle Comets, France Mentré, Niels Hendrickx, +7 more
3citations