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Quality of Conduct and Reporting of Propensity Score Methods in Studies Investigating the Effectiveness of Antimicrobial Therapy2022 Open Forum Infectious Diseases article Mathematics Advanced Causal Inference Techniques Open access
Anna M. Eikenboom, Saskia le Cessie, Ingeborg Waernbaum, Rolf H. H. Groenwold, Mark G. J. de Boer
10citations -
The Changing Face of Oncology Research, Drug Development, and Clinical Practice: Toward Patient‐Focused Precision Therapeutics2020 Clinical Pharmacology & Therapeutics article Mathematics Statistical Methods in Clinical Trials Open access
Karthik Venkatakrishnan, Piet H. van der Graaf, Sarah A. Holstein
4citations -
The role of the estimand framework in the analysis of patient-reported outcomes in single-arm trials: a case study in oncology2024 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Doranne Thomassen, Satrajit Roychoudhury, Cecilie Delphin Amdal, Dries Reynders, Jammbe Z. Musoro, Willi Sauerbrei, +32 more
13citations -
Critical appraisal of combination therapies: the impact of trial design on benefit-risk outcomes2026 JNCI Journal of the National Cancer Institute article Mathematics Statistical Methods in Clinical Trials
Floor de Jong, Li-Anne H Douma, Paul Baas, Cornedine Jannette de Gooijer, Hans A. J. Gelderblom, Jacobus A. Burgers, +1 more
0citations -
Handling missing values in patient-reported outcome data in the presence of intercurrent events2025 BMC Medical Research Methodology article Mathematics Statistical Methods and Bayesian Inference Open access
Doranne Thomassen, Satrajit Roychoudhury, Cecilie Delphin Amdal, Dries Reynders, Jammbe Z. Musoro, Willi Sauerbrei, +31 more
13citations -
Optimizing study design in LPS challenge studies for quantifying drug induced inhibition of TNFα response: Did we miss the prime time?2022 European Journal of Pharmaceutical Sciences article Mathematics Statistical Methods in Clinical Trials Open access
Julia Larsson, Edmund Hoppe, Michael Gautrois, Marija Cvijović, Mats Jirstrand
1citations
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