Papers matching “clinical trial endpoints” 21
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The impact of allocation bias on test decisions in clinical trials with multiple endpoints using multiple testing strategies2024 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Stefanie Schoenen, Nicole Maria Heussen, Johan Verbeeck, R.-D Hilgers
6citations -
Multi-stakeholder sessions on major innovation topics in rare disease clinical trials2024 Orphanet Journal of Rare Diseases article Mathematics Statistical Methods in Clinical Trials Open access
Daniel Bodden, Stefanie Schoenen, Stephanie Wied, Johan Verbeeck, Maya Dirani, Nicole Maria Heussen, +3 more
3citations -
Istore: a project on innovative statistical methodologies to improve rare diseases clinical trials in limited populations2024 Orphanet Journal of Rare Diseases article Mathematics Statistical Methods in Clinical Trials Open access
Stefanie Schoenen, Johan Verbeeck, Lukas Koletzko, Isabella Brambilla, Mathieu Kuchenbuch, Maya Dirani, +5 more
6citations -
A first step towards best practice recommendations for the design and statistical analyses of pragmatic clinical trials: A modified Delphi approach2022 British Journal of Clinical Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Victoria Palin, Tjeerd Pieter van Staa, Stephanie Steels, Andrea B. Troxel, Rolf H. H. Groenwold, Thomas MacLennan MacDonald, +7 more
6citations -
Procedure for pooling clinical outcome data from DRUP-like clinical trials using the OMOP model.2025 Journal of Clinical Oncology conference-abstract Mathematics Statistical Methods in Clinical Trials
T.M. Kringelbach, Gro Live Fagereng, Gabriel Bratseth Stav, Maria Martin Agudo, Soemeya F. Haj Mohammad, Florentine A.J. Verbeek, +13 more
0citations -
A Knowledge Base of Designs and Statistical Methods for Adaptive Clinical Dose‐Finding Trials2026 Pharmaceutical Statistics article Mathematics Statistical Methods in Clinical Trials Open access
Rob Kessels, Yongxi Long, René Spijker, Ewoud Schuit, Marieke J Hollestelle, Chris van Lieshout, +3 more
0citations -
A Pharmacometrics‐Informed Trial Simulation Framework for Optimizing Study Designs for Disease‐Modifying Treatments in Rare Neurological Disorders2025 CPT Pharmacometrics & Systems Pharmacology article Mathematics Statistical Methods in Clinical Trials Open access
Yevgen V. Ryeznik, R.-D Hilgers, Nicole Maria Heussen, Emmanuelle Comets, France Mentré, Niels Hendrickx, +7 more
3citations -
Endpunkte zu mikrovaskulären Folgekomplikationen: klinische Endpunkte, patientenberichtete Endpunkte und Surrogatendpunkte, Methodik von Surrogatvalidierungsstudien2023 Diabetologie und Stoffwechsel article Mathematics Statistical Methods in Clinical Trials Open access
Baptist Gallwitz, Monika Kellerer, Dirk Müller‐Wieland, Christoph Wanner, Focke Ziemssen
0citations -
The role of the estimand framework in the analysis of patient-reported outcomes in single-arm trials: a case study in oncology2024 BMC Medical Research Methodology article Mathematics Statistical Methods in Clinical Trials Open access
Doranne Thomassen, Satrajit Roychoudhury, Cecilie Delphin Amdal, Dries Reynders, Jammbe Z. Musoro, Willi Sauerbrei, +32 more
13citations -
Information about missing patient-reported outcome data in breast cancer trials is frequently not documented: a scoping review2023 Journal of Clinical Epidemiology article Mathematics Statistical Methods in Clinical Trials Open access
Daniela Krepper, Johannes Maria Giesinger, Linda Dirven, Fabio Efficace, Caroline Lopes Martini, Anna Margarete Maria Thurner, +3 more
12citations -
Tell me what you want, what you really really want: Estimands in observational pharmacoepidemiologic comparative effectiveness and safety studies2023 Pharmacoepidemiology and Drug Safety article Mathematics Statistical Methods in Clinical Trials Open access
Kim Luijken, Rik van EEKELEN, Helga Gardarsdóttir, Rolf H. H. Groenwold, Nan van Geloven
21citations
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