September 23, 2026 preprint Open access A Generalizable, Governance-Embedded Pathway for Assessing Patient-Level Opportunities for Genetic Medicines medRxiv DOI: 10.64898/2026.09.22.26363712 Full text (OA) OpenAlex Authors 0 Author list not loaded yet. Cited by 0 stored of 0 References 6 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Possibilities and limitations of antisense oligonucleotide therapies for the treatment of monogenic disorders 2024 Communications Medicine article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access cited by 5 patents 272 citations The N=1 Collaborative: advancing customized nucleic acid therapies through collaboration and data sharing 2025 Nucleic Acids Research article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access 25 citations Joining forces to develop individualized antisense oligonucleotides for patients with brain or eye diseases: the example of the Dutch Center for RNA Therapeutics 2024 Therapeutic Advances in Rare Disease article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access 9 citations Screening rare genetic diagnoses for amenability to bespoke antisense oligonucleotide therapy development: A retrospective cohort study 2025 Genetics in Medicine article Biochemistry, Genetics and Molecular Biology Genomics and Rare Diseases 4 citations Interventional genomics: Bridging germline diagnosis and therapeutic action 2026 Genetics in Medicine article Biochemistry, Genetics and Molecular Biology Genomics and Rare Diseases 3 citations Guidance on communication and informed consent with patients and their families for experimental individualized treatments 2026 The American Journal of Human Genetics article Medicine Ethics in Clinical Research Open access 1 citations 6 results