April 25, 2025 article Open access Unlocking the future: Precision oligonucleotide therapy for targeted treatment of neurodegenerative disorders International Journal of Biological Macromolecules DOI: 10.1016/j.ijbiomac.2025.143515 Full text (OA) OpenAlex Authors 0 Author list not loaded yet. Cited by 0 stored of 4 References 2 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Exon 1-targeting miRNA reduces the pathogenic exon 1 HTT protein in Huntington's disease models 2024 Brain article Neuroscience Genetic Neurodegenerative Diseases Open access 26 citations Solution Oligonucleotide APIs: Regulatory Considerations 2022 Therapeutic Innovation & Regulatory Science article Immunology and Microbiology Biosimilars and Bioanalytical Methods Open access 10 citations 2 results