November 21, 2019 article Open access Noncompletion and nonpublication of trials studying rare diseases: A cross-sectional analysis PLoS Medicine DOI: 10.1371/journal.pmed.1002966 Full text (OA) OpenAlex Authors 0 Author list not loaded yet. Cited by 4 stored of 111 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access Digital health technology use in clinical trials of rare diseases: a systematic review 2025 Communications Medicine review Health Professions Mobile Health and mHealth Applications Open access 5 citations Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases—A secondary analysis of a randomized clinical trial 2024 PLoS ONE article Mathematics Statistical Methods in Clinical Trials Open access 2 citations Istore: a project on innovative statistical methodologies to improve rare diseases clinical trials in limited populations 2024 Orphanet Journal of Rare Diseases article Mathematics Statistical Methods in Clinical Trials Open access 6 citations Publication rates in small German trials remained low five years after trial completion 2022 Contemporary Clinical Trials article Decision Sciences Meta-analysis and systematic reviews Open access 6 citations 4 results References 0