February 02, 2015 article Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers Nature Medicine DOI: 10.1038/nm.3765 OpenAlex Authors 0 Author list not loaded yet. Cited by 8 stored of 332 Search Sort Most cited Newest Oldest Patent citations Title Any typearticle review book-chapter conference-paper preprint dissertation book dataset other Any fieldAgricultural and Biological Sciences Arts and Humanities Biochemistry, Genetics and Molecular Biology Business, Management and Accounting Chemical Engineering Chemistry Computer Science Decision Sciences Dentistry Earth and Planetary Sciences Economics, Econometrics and Finance Energy Engineering Environmental Science Health Professions Immunology and Microbiology Materials Science Mathematics Medicine Neuroscience Nursing Pharmacology, Toxicology and Pharmaceutics Physics and Astronomy Psychology Social Sciences Veterinary Open access RNA therapies are delivering as therapies for neuromuscular dystrophy patients: Editorial for the special issue on RNA therapies in Journal of Neuromuscular Diseases 2025 Journal of Neuromuscular Diseases editorial Medicine Neurogenetic and Muscular Disorders Research Open access 0 citations Understanding Duchenne muscular dystrophy-associated brain pathology 2025 Disease Models & Mechanisms article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 2 citations Nanomedicine for Treating Muscle Dystrophies: Opportunities, Challenges, and Future Perspectives 2022 International Journal of Molecular Sciences article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 19 citations 7′,5′-alpha-bicyclo-DNA: new chemistry for oligonucleotide exon splicing modulation therapy 2021 Nucleic Acids Research article Biochemistry, Genetics and Molecular Biology DNA and Nucleic Acid Chemistry Open access 11 citations Developments in reading frame restoring therapy approaches for Duchenne muscular dystrophy 2020 Expert Opinion on Biological Therapy article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 25 citations 249th ENMC International Workshop: The role of brain dystrophin in muscular dystrophy: Implications for clinical care and translational research, Hoofddorp, The Netherlands, November 29th–December 1st 2019 2020 Neuromuscular Disorders article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access 32 citations Premature termination codons in the DMD gene cause reduced local mRNA synthesis 2020 Proceedings of the National Academy of Sciences article Biochemistry, Genetics and Molecular Biology Muscle Physiology and Disorders Open access cited by 2 patents 80 citations Opportunities and challenges for antisense oligonucleotide therapies 2020 Journal of Inherited Metabolic Disease article Biochemistry, Genetics and Molecular Biology RNA Interference and Gene Delivery Open access cited by 1 patent 155 citations 8 results References 0